| Rank | Logo | Company | Market Cap | Country |
|---|---|---|---|---|
| 1 | Krystal Biotech | $7.54 B | USA | |
| 2 | CRISPR Therapeutics | $4.50 B | Switzerland | |
| 3 | Beam Therapeutics | $2.56 B | USA | |
| 4 | Intellia Therapeutics | $1.55 B | USA | |
| 5 | Taysha Gene Therapies | $1.24 B | USA | |
| 6 | Oxford Biomedica | $1.00 B | UK | |
| 7 | uniQure | $0.95 B | Netherlands | |
| 8 | Prime Medicine | $0.66 B | USA | |
| 9 | MeiraGTx | $0.59 B | USA | |
| 10 | enGene | $0.48 B | Canada | |
| 11 | Benitec Biopharma | $0.39 B | USA | |
| 12 | Neurogene | $0.29 B | USA | |
| 13 | Editas Medicine | $0.22 B | USA | |
| 14 | Voyager Therapeutics | $0.22 B | USA | |
| 15 | Sangamo Therapeutics | $0.12 B | USA | |
| 16 | Korro Bio | $0.10 B | USA | |
| 17 | Passage Bio | $23.67 M | USA | |
| 18 | GenSight Biologics | $21.4 M | France | |
| 19 | Genprex | $4.35 M | USA |
Largest gene therapy companies by Market Cap




